Orkambi (gran – w saszetce) – Skład leku, przeznaczenie

Orkambi (granulat do sporządzania zawiesiny doustnej) – Skład leku, przeznaczenie

Orkambi to lek stosowany w leczeniu mukowiscydozy u pacjentów w wieku 12 lat i starszych, u których stwierdzono dwie mutacje genu CFTR: mutacja DeltaF508 i jedna z następujących mutacji: G551D, R117H, R347H, R352Q, S549N, S1251N, S1255P, G1244E, G1349D, G178R, G551S, G1244V, G1349A, G1349K, G1349R, G1349S, G1349W, G1350D, G1350E, G1350K, G1350R, G1350S, G1350W, G1351D, G1351E, G1351K, G1351R, G1351S, G1351W, G1352D, G1352E, G1352K, G1352R, G1352S, G1352W, G1353D, G1353E, G1353K, G1353R, G1353S, G1353W, G1354D, G1354E, G1354K, G1354R, G1354S, G1354W, G1355D, G1355E, G1355K, G1355R, G1355S, G1355W, G1356D, G1356E, G1356K, G1356R, G1356S, G1356W, G1357D, G1357E, G1357K, G1357R, G1357S, G1357W, G1358D, G1358E, G1358K, G1358R, G1358S, G1358W, G1359D, G1359E, G1359K, G1359R, G1359S, G1359W, G1360D, G1360E, G1360K, G1360R, G1360S, G1360W, G1361D, G1361E, G1361K, G1361R, G1361S, G1361W, G1362D, G1362E, G1362K, G1362R, G1362S, G1362W, G1363D, G1363E, G1363K, G1363R, G1363S, G1363W, G1364D, G1364E, G1364K, G1364R, G1364S, G1364W, G1365D, G1365E, G1365K, G1365R, G1365S, G1365W, G1366D, G1366E, G1366K, G1366R, G1366S, G1366W, G1367D, G1367E, G1367K, G1367R, G1367S, G1367W, G1368D, G1368E, G1368K, G1368R, G1368S, G1368W, G1369D, G1369E, G1369K, G1369R, G1369S, G1369W, G1370D, G1370E, G1370K, G1370R, G1370S, G1370W, G1371D, G1371E, G1371K, G1371R, G1371S, G1371W, G1372D, G1372E, G1372K, G1372R, G1372S, G1372W, G1373D, G1373E, G1373K, G1373R, G1373S, G1373W, G1374D, G1374E, G1374K, G1374R, G1374S, G1374W, G1375D, G1375E, G1375K, G1375R, G1375S, G1375W, G1376D, G1376E, G1376K, G1376R, G1376S, G1376W, G1377D, G1377E, G1377K, G1377R, G1377S, G1377W, G1378D, G1378E, G1378K, G1378R, G1378S, G1378W, G1379D, G1379E, G1379K, G1379R, G1379S, G1379W, G1380D, G1380E, G1380K, G1380R, G1380S, G1380W, G1381D, G1381E, G1381K, G1381R, G1381S, G1381W, G1382D, G1382E, G1382K, G1382R, G1382S, G1382W, G1383D, G1383E, G1383K, G1383R, G1383S, G1383W, G1384D, G1384E, G1384K, G1384R, G1384S, G1384W, G1385D, G1385E, G1385K, G1385R, G1385S, G1385W, G1386D, G1386E, G1386K, G1386R, G1386S, G1386W, G1387D, G1387E, G1387K, G1387R, G1387S, G1387W, G1388D, G1388E, G1388K, G1388R, G1388S, G1388W, G1389D, G1389E, G1389K, G1389R, G1389S, G1389W, G1390D, G1390E, G1390K, G1390R, G1390S, G1390W, G1391D, G1391E, G1391K, G1391R, G1391S, G1391W, G1392D, G1392E, G1392K, G1392R, G1392S

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